Development of Molecular Targeted and Nucleic Acid Therapeutics for C11orf97
Erythromycin binds to CUG-expanded RNA to suppress RNA toxicity and splicing misregulation in DM1.
Life-extending effects confirmed in mice by using the sensor molecule CtBP2, which has broad metabol…
Upstream Stop Codon Insertion to Suppress CAG Repeat–Driven Disease Progression
An electricity-free pump powered by shaking motion automatically supplies gas, while a specialized p…
Suppression of epidermal cell death through control of necroptosis by chenodeoxycholic acid
This page is currently available only in Japanese.
This page is currently available only in Japanese.
Membrane vesicles encapsulating enzymes formed by microorganisms act as electrocatalysts to generate…
Suitable for patients with comorbidities